Rare Diseases



Here and Now: Inspiring Stories of Cancer Survivors --
by Elena Dorfman, Heidi Schultz Adams
Kathy's Hats: A Story of Hope Kathy's Hats: A Story of Hope
by Trudy Krisher
My Mommy's Cancer
by Cindy Klein Cohen
Beating Cancer With Nutrition
by Patrick Quillin
A Cancer Battle Plan: Six Strategies for Beating Cancer, from a Recovered "Hopeless Case"
by Anne E. Frahm, David J. Frahm
How to Fight Cancer & Win
by William L. Fischer
What to Eat if You Have Cancer
by Daniella Chace
The Cure for All Cancers: Including over 100 Case Histories of Persons Cured
by Hulda Regehr Clark
Just Get Me Through This: The Practical Guide to Breast Cancer
by Deborah A. Cohen

    Rare Diseases





    [an error occurred while processing this directive] Controversy over source of harvested human eggs highlights ... Nov 22, 2005
    ...can overcome the ethical problems through voluntary donation, with this foundation," said Shin Hyun Min, president of the Korean Organization for Rare Diseases ...
    - OhmyNews International,

    OPi Launches Erwinase in the UK Through its Newly Formed UK ... Nov 22, 2005
    OPi, Pharmaceuticals for Rare Diseases, and the Health Protection Agency (HPA) announce today that Erwinase® (crisantaspase), L-asparaginase derived from ...
    - PharmaLive.com (press release),

    Treatment pledged for rare diseases Oct 23, 2005
    By MIKE OLIVEIRA, CP. TORONTO -- Sufferers of the rare ailments Fabrys disease and MPS-1 got some good news yesterday with the announcement ...
    - London Free Press,

    Should drugs for rare diseases be given special status in the NHS? Oct 27, 2005
    The growing number and costs of drugs for rare diseases (orphan drugs) are straining healthcare budgets. Should the NHS continue ...
    - EurekAlert (press release),

    Boost for patients with rare diseases Oct 23, 2005
    By CP. TORONTO -- Sufferers of the rare ailments Fabrys disease and MPS-1 got some good news yesterday with the announcement that ...
    - Ottawa Sun,

    Call for increase in flu vaccines Nov 17, 2005
    Italian and US health officials signed an accord to strengthen cooperation between their two countries in tackling cancer, bioterrorism and rare diseases. ...
    - Ireland Online,

    Gene Knockout Scores a Fearless Mouse Nov 22, 2005
    ...and supporting basic, clinical, and translational medical research, and it investigates the causes, treatments, and cures for both common and rare diseases. ...
    - National Institutes of Health (press release)

    Accredo Completes Acquisition of Specialty Pharmacy Business Nov 21, 2005
    ..."The strategic acquisition of PSAI's assets expands our leadership position in the treatment and care of pediatric patients with rare diseases, such as ...
    - PR Newswire (press release),

    Patients, Industry and Lawmakers Seek to End SBA Bureaucratic ... Nov 9, 2005
    ..."Patients with rare diseases, such as cystic fibrosis, often rely on small biotech companies to develop new treatments to save their lives. ...
    - PR Newswire (press release),

    A biotech drug extends a life, but at what price? Nov 16, 2005
    Using incentives passed by Congress to encourage the development of medicine for rare diseases, Genzyme Corp., then a tiny company, brought the drug to market ...
    - Pittsburgh Post Gazette,

    Daily Policy Digest Nov 17, 2005
    ..."Orphan" medications -- treatments for rare diseases -- have become an unlikely source of revenue for pharmaceutical companies, says the Wall Street Journal. ...
    - National Center for Policy Analysis,

    FDA Approves Arranon For Rare Leukemia and Lymphoma Nov 16, 2005
    Arranon also received Orphan Drug Designation, which is granted to products that treat rare diseases (those that affect fewer than 200,000 people in the United ...
    - Pharmaceutical Processing,

    Chief Scientist: Genzyme mulling Israeli R&D center Nov 17, 2005
    Scientist Eli Opper said today. Genzyme focuses on developing drugs for treatment of rare diseases (orphan drugs). During a recent visit ...
    - Globes,

    Atyrau (Kazakhstan), Moscow (Russia) held medicine telebridge Nov 21, 2005
    Neurosurgeon Institute named after Burdenko and National Cardiovascular Medicine Center named after Bakulev consulted people, suffering from rare diseases. ...
    - Kazinform,

    Rare Disorder Patients Face Access Restrictions on Expensive ... Nov 9, 2005
    This is not sound medicine." Because of the low prevalence rates of rare diseases, many important clinical events that vary by dosing regimen or brand are ...
    - Genetic Engineering News,

    Wall Street Journal Examines High Price of Gaucher Disease ... Nov 16, 2005
    Under the Orphan Drug Act, passed in 1983 to encourage the development of treatments for rare diseases, pharmaceutical and biotechnology companies can market ...
    - Kaiser network.org,

    Zoek in het archief Oct 27, 2005
    ...( BW)(EPPOSI) Pharma, Government and Patients Come Together in Aid of Rare Diseases; Stakeholders Speak Out on the Huge Unmet Need in the Funding, Research and ...
    - Netherlands Corporate News,

    Health Net Gives a Boy Access to Specialist Care After Lawsuit Nov 9, 2005
    But others with rare diseases often face similar battles with their HMOs, said Mary Dunkle, a spokeswoman for the Connecticut-based National Organization for ...
    - Los Angeles Times,

    Pharma, Government and Patients Come Together in Aid of Rare ... Oct 27, 2005
    27, 2005--One in 33 babies is born with a rare genetic disease - most of which have no cure(1). Yet the burden of rare diseases is immense and affects over 30 ...
    - Business Wire (press release),

    Genetic Catalog May Aid Search for Roots of Disease Oct 26, 2005
    Unlike rare diseases, which tend to be caused by a single gene with a clear family pedigree, common diseases like cancer and diabetes probably spring from ...
    - New York Times,

    Fearing avian flu, US scrambles to fill drug gap Nov 10, 2005
    ...same disease for a decade. So-called orphan drugs for rare diseases already enjoy seven years of protection. The bill also calls ...
    - Pittsburgh Post Gazette,

    Discovery Labs' Surfaxin Granted Orphan Drug Designation for the ... Oct 28, 2005
    The US Orphan Drug Act is intended to assist and encourage companies to develop safe and effective therapies for the treatment of rare diseases and disorders. ...
    - PharmaLive.com (press release),

    Boy's case draws rare light to HMO Nov 13, 2005
    Jack's parents said they hoped his case would help others with rare diseases. "Our first concern is for Jack," his mother said. ...
    - Contra Costa Times,

    CHEO tapped for newborn tests Nov 2, 2005
    Medical Centre. The tests will detect rare diseases that can cause serious health problems and even be fatal. Developmental delays ...
    - Ottawa Sun,

    Bizarre Trip of a Lifetime Nov 11, 2005
    Flying in an Ilyushin does not count. For an adventure traveler, it's not a trip unless it involves sweat, scratches and the possibility of rare diseases. ...
    - Los Angeles Times,

    You Scored a North Korea Travel Visa? Hold Everything! Nov 11, 2005
    Flying in an Ilyushin does not count. For an adventure traveler, it’s not a trip unless it involves sweat, scratches and the possibility of rare diseases. ...
    - World Hum,

    Geneticists map what makes us different Oct 27, 2005
    ...a powerful tool that enables biologists to study the root causes of disease, but most of the disease genes found so far are single genes linked to rare diseases ...
    - Boston Globe,

    Free-for-all over generic drugs Nov 15, 2005
    ...and their work" because governments often neglect members of groups like his who are fighting for better care for patients with rare diseases or, say, serious ...
    - International Herald Tribune,

    Ariad Gets 'Orphan Drug' Label in Europe Nov 15, 2005
    The orphan drug label, reserved for new therapies for rare diseases, means Ariad could have 10 years of exclusive selling rights in Europe along with reduced ...
    - Forbes

    New DNA study could change the face of medicine Oct 27, 2005
    ...week. But the report quoted some experts as saying that HapMap told only "half the story" as it could not be used for rare diseases.
    - Webindia123,

    Newton history book tells a tale of stubborn survival Nov 13, 2005
    But the tidbits that stand out the most are about mischievous animals, freak accidents and rare diseases, rather than tales of civic pride. ...
    - Charlotte Observer,

    NC State Receives Funding to Develop New Drug-Discovery Methods Nov 15, 2005
    More importantly, it would. make drug-discovery efforts for rare diseases more cost-effective for pharmaceutical companies to pursue. ...
    - dBusinessNews Triangle (press release),

    MEDICINE MENSCH: What Little I Know About Medicine Nov 9, 2005
    ...irrelevant, by practical considerations. On the other hand, you don't want to miss the rare diseases when they do pop up. So both kinds ...
    - Forward,

    10 medical missions and more for Emergency’s 10th anniversary Nov 9, 2005
    ...parts of the country; facilitated numerous operations for indigents; in-formed the public and authorities about new and rare diseases, medical breakthroughs ...
    - Tempo,

    Biomed Rounds: Genzyme seems immune to condition plaguing ... Nov 14, 2005
    ...case studies are made. The company, launched in 1981, targeted rare diseases that big pharma chose to ignore. The company was able ...
    - Boston Mass High Tech,

    Gene map points to personal drugs Oct 26, 2005
    ...as diabetes. But some experts said HapMap, detailed in Nature, told "half the story" as it could not be used for rare diseases.
    - LaSalute.net,

    A Doctor for the Future Nov 5, 2005
    ..."'Medical genetics' conjures up visions of rare diseases that are only of interest to a few people," he says. "'Genetic medicine' tells it the way it is. ...
    - New York Times,

    Family fights an HMO for 4-year-old's life Nov 5, 2005
    Zembsch says. "Jack fits into the category of you-can't-believe-it rare.''. HMOs never want to hear about rare diseases. And the ...
    - San Francisco Chronicle,

    UPDATE 1-Astra drug wins "orphan" status for thyroid cancer Oct 31, 2005
    Orphan status, which carries with it seven years of market exclusivity under US rules, is granted to promote the development of medicines for rare diseases. ...
    - Reuters

    Shire Has 3rd-Qtr Loss on Write Off of Research (Update3) Nov 3, 2005
    Emmens bought Transkaryotic for $1.6 billion to gain treatments for anemia and rare diseases and reduce reliance on Adderall XR, which accounts for half of ...
    - Bloomberg

    Kid's Clothing ReSale bigger success than last year Oct 28, 2005
    Monies raised from the ReSale event will be donated to organizations supporting children with rare disease or directly to children suffering from rare diseases ...
    - Canton Journal,

    Shire Has 3rd-Qtr Loss on Write Off of Research (Update2) Nov 3, 2005
    ...for $1.6 billion to gain treatments for anemia and rare diseases and reduce reliance on Adderall XR, which accounts for half of sales at the company. ...
    - Bloomberg

    FDA Grants AstraZeneca Orphan-Drug Designation for ZACTIMA (ZD6474 ... Oct 31, 2005
    ...drug designation was designed to promote the development of products that demonstrate promise for the diagnosis and/or treatment of rare diseases or conditions ...
    - Yahoo! News (press release)

    Discovery Laboratories treatment gets key status Oct 28, 2005
    Orphan drug designation is awarded to compounds that offer potential therapeutic value in the treatment of rare diseases, defined as those affecting fewer than ...
    - Philadelphia Business Journal,

    Protect UAW Retirees: Their Future Is Our Future Oct 26, 2005
    For example, will the plan discriminate against the mentally or chronically ill or people with rare diseases by limiting or denying coverage? ...
    - Monthly Review,

    TriHealth of Ohio Selects Emergisoft as Emergency Department ... Oct 24, 2005
    Syndromic surveillance has become increasingly important for local, state and federal health agencies to track not only rare diseases and events, but also ...
    - Business Wire (press release),

    Talecris Biotherapeutics Showcases Its Clayton Facility to State ... Nov 4, 2005
    ...the only state-of-the-art facility in the region completely dedicated to the production of therapeutic proteins that treat rare diseases, including immune ...
    - Business Wire (press release),

    Norvartis seeks closer ties with Israel’s R&D community Nov 1, 2005
    ...trials because of the international experience of its medical community; the broad ethnic diversity of its population; the presence of rare diseases unique to ...
    - Globes,

    What rare diseases can teach us Sep 3, 2005
    ...more to fund rare-disease research. First, even rare diseases affect a huge number of people. Nearly 25 million Americans suffer ...
    - Los Angeles Times

    National Children’s Study Announces Contracts to First Research ... Sep 29, 2005
    ...and supporting basic, clinical, and translational medical research, and it investigates the causes, treatments, and cures for both common and rare diseases. ...
    - National Institutes of Health (press release)

    CepTor Announces Patent Filing for Neurodur (C-201) Pro-Drug in ... Sep 30, 2005
    ...seeks to create an efficient orphan drug platform by taking advantage of the legislative, regulatory and commercial opportunities common to these rare diseases ...
    - Genetic Engineering News

    First international meeting on bone marrow diseases Oct 1, 2005
    The symposium is sponsored by the National Institutes of Health, including the Office of Rare Diseases, the National Heart, Lung and Blood Institute and the ...
    - Medical News Today (press release)

    Insmed reports positive drug trial Sep 30, 2005
    ...month, Tercica received "orphan drug" status from the FDA, which gives the company seven years of market exclusivity to promote treatments for rare diseases. ...
    - Richmond Times Dispatch

    Insmed Says Drug Increased Growth Speed Sep 29, 2005
    The FDA uses orphan drug status, which carries seven years of exclusive selling rights, to motivate companies to develop treatments for rare diseases. ...
    - MSN Money

    Novartis, new products portfolio Oct 1, 2005
    Gleevec is on track to be submitted by the end of 2005 in the US, EU and Japan as a treatment for Ph+ acute lymphoid leukemia ( ALL ) and other rare diseases. ...
    - Xagena.it

    Rash impact Sep 19, 2005
    The most common explanation provided was that it is very difficult and time consuming to gather statistical data about rare diseases because they don't fall ...
    - Grand Forks Herald

    Girl riding to combat rare disease Sep 28, 2005
    Mace said. ""It's such a rare or orphan disease it's not even listed yet on the national organization of rare diseases web site. I ...
    - Westlake West Life

    Victims of rare disease remain positive despite daily challenges Sep 23, 2005
    ...“There are probably more than 6,000 rare diseases and we’re all trying to inform the public about our particular diseases,� Parent said. ...
    - Rockford Register Star

    Fabry Society Anticipates Approval of Orphan Drug Policy and ... Sep 1, 2005
    ...sent letters to Federal Health Minister Ujjah Dosanjh, urging Health Canada to provide access to potentially life-saving drugs for patients with rare diseases. ...
    - Canada NewsWire (press release)

    Novartis Presents Positive Phase III Data on Key Compounds and ... Sep 19, 2005
    Gleevec is on track to be submitted by the end of 2005 in the US, EU and Japan as a treatment for Ph+ acute lymphoid leukemia (ALL) and other rare diseases. ...
    - PrimeZone (press release)

    DR. BROBSON LUTZ: Beware of myths, but health risks are real Sep 9, 2005
    As we move forward, the endemic health problems will not be strange and rare diseases. We will have endemic cuts, lacerations and puncture wounds. ...
    - Times Picayune

    The doctor is back in the “House� Sep 23, 2005
    House" features Doctor Gregory House (British actor Hugh Laurie) who, with the help of his co-workers, treats patients suffering from obscure and rare diseases ...
    - Silver Chips Online

    OPi and the UK Health Protection Agency (HPA) Enter Into a World ... Aug 30, 2005
    Rights for Erwinase(R) (Crisantaspase) LYON, France, and PORTON DOWN, England, August 30 /PRNewswire/ -- OPi SA, Pharmaceuticals for Rare Diseases and the UK ...
    - PR Newswire (press release)

    Insmed's drug approval may be near Sep 28, 2005
    The agency granted Tercica "orphan drug" status, which gives seven years of market exclusivity to promote treatments for rare diseases. ...
    - Richmond Times Dispatch

    OPi and the UK Health Protection Agency (HPA) Enter Into a World ... Aug 30, 2005
    30 /CNW/ - OPi SA, Pharmaceuticals for Rare Diseases and the UK Health Protection Agency (HPA) announce today that they have entered into a world-wide ...
    - ArriveNet (press release)

    OPi and the UK Health Protection Agency (HPA) Enter Into a World ... Aug 30, 2005
    LYON, France, and PORTON DOWN, England, August 30 /PRNewswire/ -- OPi SA, Pharmaceuticals for Rare Diseases and the UK Health Protection Agency (HPA) announce ...
    - Yahoo News (press release)

    2 deer test negative for wasting disease Sep 8, 2005
    Test results for eastern equine encephalitis and West Nile disease are expected in another week. "Those are very rare diseases. ...
    - MLive.com

    Nabi Biopharmaceuticals Receives Favorable Opinion From the ... Sep 22, 2005
    Commission later this year. OMP designation is reserved for medicines being developed for rare diseases. Orphan medicinal products ...
    - PR Newswire (press release)

    Taking a Stand Sep 2, 2005
    Sarah's underlying conditions are among the 6,000 or so rare diseases in the United States that don't typically draw much attention from biotechnology and ...
    - Baltimore Sun

    Fighting back at ALS Sep 14, 2005
    If our venture really succeeds, and we discover that first drug, we can do the same thing for patients suffering from other rare diseases.�. ...
    - Globes

    Mixed Message for MS Patients Sep 16, 2005
    Schering. Genzyme, based in Cambridge, Mass., bought Ilex to add cancer drugs to its line-up of medications for rare diseases. The ...
    - TheStreet.com

    EU assembly votes for drug patent extension Sep 7, 2005
    Standard drug patents in Europe last for 15 years except for so-called "orphan drugs" -- drugs to treat rare diseases, which generate little revenue. ...
    - Reuters AlertNet

    EPIX Pharmaceuticals Appoints Michael Astrue as Interim CEO Sep 14, 2005
    Officer of Transkaryotic Therapies in Cambridge, Mass., a biopharmaceutical company with major focus on developing products for the treatment of rare diseases. ...
    - PR Newswire (press release)

    Republicans must keep focus on woes caused by illegal immigration Aug 29, 2005
    Contagious diseases that our country wiped out years ago, such as malaria, polio, tuberculosis, and hepatitis, and rare diseases of Third World poverty such as ...
    - Town Hall

    Conference on post-market drug safety and effectiveness Sep 12, 2005
    The five focus areas are: - "Real world" drug safety and effectiveness - Catastrophic drug coverage - Expensive drugs for rare diseases - Common drug formulary ...
    - CNW Telbec (Communiqués de presse)

    AmpliMed anticancer drug given expanded orphan status Sep 2, 2005
    ...application user fee. These advantages are intended to encourage sponsors to develop drugs for patients with rare diseases. 22,200 new ...
    - Pharmaceutical Business Review

    Massey dog experiments 'scientifically dubious' Aug 29, 2005
    An anti vivisection group says Massey Universities research into rare diseases using dogs is scientifically flawed. Massey University ...
    - Scoop.co.nz (press release)

    Drug Approval Boosts Tercica Aug 31, 2005
    ...deficiency. Orphan-drug status is granted for drugs made for rare diseases, and allows for exclusive marketing rights and tax credits. ...
    - TheStreet.com

    Rare Diseases Mean Solid Growth for GenzymeJul 18, 2005
    By plying its research efforts in the direction of treatments for rare diseases with few (if any) existing treatments, Genzyme has not only largely sidestepped ...
    - MSNBC

    Beacon Hill briefsJul 27, 2005
    Concerned that rare diseases could be used for bioterrorism, the state Department of Public health is poised to add two new diseases to a list of illnesses ...
    - Wilmington Advocate

    Local briefs (Walpole)Jul 28, 2005
    Rare Kids, Inc. is a nonprofit organization established to support children afflicted with rare diseases. Over the past three years ...
    - Daily News Transcript

    $1.6B Biopharma Deal ApprovedJul 27, 2005
    ...firm’s $1.6-billion sale to Britain ’s Shire Pharmaceuticals Wednesday in a move that gives Shire access to key drugs for treating rare diseases caused by ...
    - Red Herring

    TKT Stockholders Approve Acquisition by ShireJul 27, 2005
    ...is a biopharmaceutical company primarily focused on researching, developing and commercializing treatments for rare diseases caused by protein deficiencies. ...
    - Yahoo News

    Donate clothing to Rare KidsJul 24, 2005
    Rare Kids, Inc. is a Walpole-based nonprofit organization established to support children afflicted with rare diseases. Over the ...
    - Daily News Transcript

    FDA Grants Bronchitol Orphan Drug Status for Treatment of Cystic ...Jul 20, 2005
    Orphan drug status is granted by the FDA to those products intended for the diagnosis, prevention and treatment of rare diseases, or conditions where no ...
    - PharmaLive.com

    Biotech TKT's Shareholders Approve SaleJul 27, 2005
    ...as the basis for a higher price and a greater return on investors' shares of Cambridge-based TKT, which is developing drugs to treat rare diseases linked to ...
    - Washington Post

    Shareholders sign on to Shire's purchase of Mass. companyJul 27, 2005
    TKT, which is based in Cambridge, Mass., is a biopharmaceutical company focusing on developing treatments for rare diseases caused by protein deficiencies. ...
    - Philadelphia Business Journal

    TKT stockholders OK acquisition by ShireJul 28, 2005
    TKT is a biopharmaceutical company focused on researching, developing and commercializing treatments for rare diseases caused by protein deficiencies. ...
    - Boston Mass High Tech

    UCB Receives Positive Opinion from European Authorities for Orphan ...Jul 25, 2005
    The EMEA, through the COMP is responsible for reviewing designation applications from sponsors who intend to develop medicines for rare diseases. ...
    - PharmaLive.com

    High Blood Pressure Not Well Controlled Among Older Men and WomenJul 27, 2005
    ...and supporting basic, clinical, and translational medical research, and investigates the causes, treatments, and cures for both common and rare diseases. ...
    - eMaxHealth.com

    Business DigestJul 28, 2005
    TKT shares. The Cambridge, Mass., biotech is developing drugs to treat rare diseases linked to protein deficiencies. MeadWestvaco ...
    - Baltimore Sun

    Novartis takes rare road to curesJul 7, 2005
    From its headquarters nestled on the Rhine in the Swiss town of Basel, Novartis is pioneering the use of rare diseases, like Muckle-Wells, as a testing ground ...
    - International Herald Tribune

    Drug treatment mimics circadian rhythmsJul 25, 2005
    Orphan status is granted to products with a limited patient population and is designed to encourage R&D into treatments for rare diseases. ...
    - in-PharmaTechnologist

    Technological advances require social advancesJul 17, 2005
    ...have created incentives for companies to engage in research and development activities that, if successful, will yield drugs to treat rare diseases (in the ...
    - Boston Globe

    Looking for CuresJul 4, 2005
    ...of Pittsburgh is making a big push into drug discovery by opening a laboratory that will focus exclusively on treatments for rare diseases, especially some ...
    - MSNBC

    Student joins cancer battleJul 22, 2005
    The National Organization for Rare Disorders (NORD), maintains a website on rare diseases and disorders, and has cataloged articles and research information on ...
    - Randolph Reporter

    DoD Releases Study on Link Between Agent Orange and DiabetesJul 15, 2005
    Second, the size of the study makes it difficult to detect increases in rare diseases, thus small increases in rare diseases may be missed by the study. ...
    - Navy Compass

    Vietnam War health study links Agent Orange and diabetesJul 17, 2005
    Second, the size of the study makes it difficult to detect increases in rare diseases; thus, small increases in rare diseases may be missed by the study. ...
    - Providence Journal (subscription)

    How newborn screening tests could changeJul 5, 2005
    The team analyzed 84 rare diseases, Watson said, but chose only those that met key criteria, including: the screening test is reliable; the disorder causes ...
    - Kansas.com

    Quarterly Profit at Novartis Increases 9% on Strong Drug Sales in ...Jul 14, 2005
    Novartis's research center in Cambridge, Mass., led by Mark Fishman, is focusing on rare diseases, hoping to speed drug development. ...
    - New York Times

    The time of his lifeJul 10, 2005
    Wendy and Rob knew nothing but a miracle could save Andrew, but both wanted to provide hope for other children with rare diseases. ...
    - Ventura County Star (subscription)

    Korean bishop issues pastoral on stem-cell researchJul 22, 2005
    ..._The bishop also addresses the question of the use of embryonal stem cells in research to treat rare diseases: He writes that the use of stem cells from ...
    - Catholic World News

    Hadassah deserves Nobel peace prizeJul 19, 2005
    Hadassah has been a worldwide leader in fighting breast cancer and other women’s diseases while seeking cures for myriad ailments, from rare diseases to the ...
    - Ynetnews

    Chemokine Therapeutics' cancer drug granted orphan-drug ...Jul 19, 2005
    The US Orphan Drug Act is intended to assist and encourage companies to develop safe and effective therapies for the treatment of rare diseases and disorders ...
    - Canada NewsWire

    School board approves health insurance mergerJul 27, 2005
    Several talked about personal struggles -- cancer treatments, surgeries and rare diseases -- and their anxiety over a change in insurance plans. ...
    - Stamford Advocate

    Diagnostic Imaging: BrainJul 21, 2005
    ...four pages. I would have preferred to see two pages allotted to the rare diseases and six allotted to the more common ones. The ...
    - Am J Roentgenology (subscription)

    Senate Finance Committee Investigating Johnson & Johnson's ...Jul 7, 2005
    According to the Times , APHS "shifted some of its focus away from the rare diseases" for which Propulsid was a treatment "and toward common childhood acid ...
    - Medical News Today

    A painful coincidenceJul 5, 2005
    ...common afflictions. Many rare diseases aren't even addressed during the four years doctors are trained in medical school. "There ...
    - Newsday

    Icahn group owns 5 percent of TranskaryoticJul 21, 2005
    Last Thursday, Transkaryotic, which develops treatments for rare diseases caused by protein deficiencies, said its board unanimously recommended that ...
    - Reuters

    Senators Ask Drug Giant to Explain Grants to DoctorsJul 5, 2005
    Dr. Hyman was a chief medical adviser to the group, which shifted some of its focus away from the rare diseases and toward common childhood acid reflux with ...
    - New York Times

    From orphan to blockbuster?Jul 8, 2005
    Drug makers used to shun treatments for rare diseases like Gaucher because they didn't generate enough sales to make the research costs worthwhile. ...
    - CNN

    The Mystery of the Shenandoah’s Ailing FishJul 15, 2005
    ...result. Fish have been sent to Pennsylvania and Virginia laboratories to be tested for rare diseases, with none found, Reeser said. ...
    - Winchester Star

    Health Canada grants Priority Review for (PR)Exjade(TM) for ...Jul 14, 2005
    The intent of the Orphan Drug designation is to stimulate the research, development, and approval of products that treat rare diseases. ...
    - Canada NewsWire

    CepTor Corporation's Proprietary Orphan Drug Development Pipeline ...Jul 13, 2005
    ...seeks to create an efficient orphan drug platform by taking advantage of the legislative, regulatory and commercial opportunities common to these rare diseases ...
    - PharmaLive.com

    Hospital treatment fees to increase from todayJul 14, 2005
    ...new regulation will not apply to patients on dialysis machines or those suffering from cancer, hemophilia, mental illness, chronic diseases and rare diseases. ...
    - Taipei Times

    ICTI Biostatistics Expert to Speak at International ConferenceJul 19, 2005
    ...vs. placebo is not possible. They are often used in studies of rare diseases, in oncology studies, and in medical device trials. Dr ...
    - PharmaLive.com

    Independence Blue Cross Launches Program to Benefit Members With ...Jul 5, 2005
    PHILADELPHIA, July 5 /PRNewswire/ -- Independence Blue Cross members with uncommon complex conditions, such as rheumatoid arthritis and multiple sclerosis, can ...
    - Yahoo News

    Firm hopes drug brings big payoffJul 13, 2005
    A once-a-day injection, SomatoKine is under "orphan drug" designation in the US The label, given to products for rare diseases -- those that affect fewer than ...
    - Richmond Times Dispatch

    UPDATE 1-Transkaryotic urges holders approve Shire dealJul 12, 2005
    TKT competes with Genzyme Corp. (GENZ.O: Quote, Profile, Research) and others in the enzyme therapy market for rare diseases. It ...
    - Reuters

    Transkaryotic Board Fights BackJul 12, 2005
    ...unlikely to be able to garner a significant acquisition premium." Considering the company specializes in developing treatments for rare diseases, there are ...
    - TheStreet.com

    Transkaryotic board recommends Shire takeoverJul 14, 2005
    Transkaryotic, which develops treatments for rare diseases caused by protein deficiencies, entered into an agreement with Britain's third-largest drugmaker in ...
    - Reuters

    Transkaryotic board recommends Shire takeoverJul 14, 2005
    Transkaryotic, which develops treatments for rare diseases caused by protein deficiencies, agreed in April to be acquired by Shire, the country's third-largest ...
    - Reuters.uk

    Genzyme shares jump on robust earningsJul 14, 2005
    Genzyme has specialized in developing niche drugs for rare diseases. The diversified biotechnology conglomerate also raised its financial outlook for 2005. ...
    - Investor's Business Daily (subscription)

    MediaSyndicate --- Free Press Release, PR, IR, News Post & Media ...Jul 7, 2005
    The Orphan Drug Act is intended to encourage development of products for rare diseases affecting fewer than 200,000 people in the United States. ...
    - MediaSyndicate

    Questcor Appoints Gregg Lapointe to Its Board of DirectorsJul 6, 2005
    ...serves on the board of EP Global Communications, Inc., and is a member of the corporate council of the National Organization for Rare Diseases (NORD), the ...
    - Business Wire

    Dissidents Emerge in Drug MergerJul 8, 2005
    Adderall XR, for attention deficit hyperactivity disorder, accounts for more than 40% of corporate sales. Transkaryotic focuses on therapies for rare diseases. ...
    - TheStreet.com

    New Spray Wipes Away SkepticismJul 9, 2005
    Or, perhaps the hormone's activity could be reduced to treat more rare diseases, like Williams syndrome, in which children have no inhibitions and approach ...
    - RedNova.com

    Medical team examines unique Peru missionJul 10, 2005
    ..."These activities put a great face on the United States and the Air Force, give me the opportunity to see rare diseases and provide an opportunity to ...
    - Blackanthem.com

    Worry-free week Young cancer patients enjoy some much-needed ...Jul 13, 2005
    ...“It kind of made me feel lucky because my illness was a common one. Some of the kids here have rare diseases,� he said. Polastre ...
    - Shamokin News Item

    High-Dose Therapy May Improve Outcome for Patients with Relapsed ...Jul 8, 2005
    Ewing’s sarcoma is one type of cancer in the Ewing’s Sarcoma Family of Tumors (ESFT)—rare diseases in which cancerous cells affect the bone and soft ...
    - Cancer Consultants

    Canada Day celebrations to be staged in TaichungJun 30, 2005
    ...there will be a charity premiere of the Canadian film "The Blue Butterfly, " to which some 200 minority children, those suffering from rare diseases and young ...
    - eTaiwan News




    This page is updated on a monthly basis if relevant articles are available. If you are looking for further information on Rare Diseases you may want to try searching the Internet using the Google search box below.


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